Search Orphan Drug Designations and Approvals
Return to Orphan Designation Search Page
|Generic Name:||arylsulfatase A (rhASA)|
|Orphan Designation:||Treatment of metachromatic leukodystrophy|
|Orphan Designation Status:||Designated|
|FDA Orphan Approval Status:||Not FDA Approved for Orphan Indication|
Shire Human Genetic Therapies, Inc.
300 Shire Way
Lexington, Massachusetts 02421
The sponsor address listed is the last reported by the sponsor to OOPD.