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U.S. Department of Health and Human Services

Search Orphan Drug Designations and Approvals
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Generic Name: peptide-oligonucleotide conjugate that targets CNOT3 mRNA
Date Designated: 10/18/2024
Orphan Designation: treatment of inherited retinal dystrophy due to PRPF31 mutations
Orphan Designation Status: Designated
FDA Orphan Approval Status: Not FDA Approved for Orphan Indication
PYC Therapeutics, LLC
112 S French Street, Suite 105
Wilmington, Delaware 19801
United States

The sponsor address listed is the last reported by the sponsor to OOPD.
*Exclusivity Protected Indications are shown for approvals from 01/01/2013 to the present.
*Data for the Date Designation Withdrawn or Revoked field are shown for designations withdrawn or revoked after 08/12/2013.
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