Search Orphan Drug Designations and Approvals
-
Generic Name: | Triheptanoin |
---|---|
Date Designated: | 02/01/2008 |
Orphan Designation: | Treatment of glycogen storage disorder II (Pompe disease) |
Orphan Designation Status: | Designated |
FDA Orphan Approval Status: | Not FDA Approved for Orphan Indication |
Sponsor: |
Baylor Research Institute 3330 Live Oak Blvd Dallas, Texas 75204 United States The sponsor address listed is the last reported by the sponsor to OOPD. |
*Data for the Date Designation Withdrawn or Revoked field are shown for designations withdrawn or revoked after 08/12/2013.
-