Search Orphan Drug Designations and Approvals
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Generic Name: | (-)-(3aR,4S,7aR)-4-Hydroxy-4-m-tolylethynyl-octahydro-indole-1-carboxylic acid methyl ester |
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Date Designated: | 10/12/2011 |
Orphan Designation: | Treatment of Fragile X syndrome |
Orphan Designation Status: | Designated |
FDA Orphan Approval Status: | Not FDA Approved for Orphan Indication |
Sponsor: |
Novartis Pharmaceuticals Corp. One Health Plaza East Hanover, New Jersey 07936 United States The sponsor address listed is the last reported by the sponsor to OOPD. |
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