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U.S. Department of Health and Human Services

Search Orphan Drug Designations and Approvals

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Generic Name: Synthetic 15-amino-acid macrocyclic peptide acylated with a ethyleneglycol palmitoylated linker
Date Designated: 07/19/2017
Orphan Designation: Treatment of paroxysmal nocturnal hemoglobinuria (PNH)
Orphan Designation Status: Designated
FDA Orphan Approval Status: Not FDA Approved for Orphan Indication
Ra Pharmaceuticals, Inc.
87 Cambridge Park Drive
Cambridge, Massachusetts 02140
United States

The sponsor address listed is the last reported by the sponsor to OOPD.

*Exclusivity Protected Indications are shown for approvals from Jan. 1, 2013, to the present.