Search Orphan Drug Designations and Approvals
-
Generic Name: | Ursodeoxycholic acid |
---|---|
Date Designated: | 04/26/2018 |
Orphan Designation: | Treatment of Niemann-Pick disease, type C |
Orphan Designation Status: | Designated |
FDA Orphan Approval Status: | Not FDA Approved for Orphan Indication |
Sponsor: |
IntraBio Inc. 270 Devon Road Tenafly, New Jersey 07670 United States The sponsor address listed is the last reported by the sponsor to OOPD. |
-