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U.S. Department of Health and Human Services

Search Orphan Drug Designations and Approvals
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Generic Name: Self complimentary adeno-associated virus serotype 9 expressing human aspartoacylase transgene
Date Designated: 12/23/2019
Orphan Designation: Treatment of Canavan Disease
Orphan Designation Status: Designated
FDA Orphan Approval Status: Not FDA Approved for Orphan Indication
Aspa Therapeutics, Inc.
421 Kipling Street
Palo Alto, California 94301
United States

The sponsor address listed is the last reported by the sponsor to OOPD.
*Exclusivity Protected Indications are shown for approvals from 01/01/2013 to the present.
*Data for the Date Designation Withdrawn or Revoked field are shown for designations withdrawn or revoked after 08/12/2013.
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