Search Orphan Drug Designations and Approvals
-
Generic Name: | Small molecule, non-isoform selective NaV persistent current inhibitor |
---|---|
Date Designated: | 04/27/2021 |
Orphan Designation: | Treatment of SCN2A Developmental and Epileptic Encephalopathy |
Orphan Designation Status: | Designated |
FDA Orphan Approval Status: | Not FDA Approved for Orphan Indication |
Sponsor: |
Praxis Precision Medicines, Inc. One Broadway, 16th Floor Cambridge, Massachusetts 02142 United States The sponsor address listed is the last reported by the sponsor to OOPD. |
*Data for the Date Designation Withdrawn or Revoked field are shown for designations withdrawn or revoked after 08/12/2013.
-